Children with SMA type 1 treated in infancy with Zolgensma alone showed motor and lung/bulbar muscle gains over two years of ...

Making a move, columnist Ari Anderson finds, can bring advantages but also complications that must be resolved.

With this extension, the SMA treatment Evrysdi is available for patients of all ages in Japan, from presymptomatic newborns ...

I’ve often said that it’s probably a good thing we don’t have a crystal ball. While sometimes it might be beneficial to know ...

Brianna Albers (she/her) is a crip-cyborg storyteller living in Minneapolis-St. Paul. She was diagnosed with spinal muscular atrophy type 2 in 1996 and lives with co-occurring physical and mental ...