DICKSON CITY, Pa. — The Eagle Hose Company in Dickson City on Saturday, November 16 hosted a benefit for the Hetzel family as ...

Gene therapy for some diseases, including Duchenne muscular dystrophy (DMD), can be tricky because the needed gene is often ...

Fill-the-Boot is a program where firefighters across the United States join forces to support the Muscular Dystrophy ...

A Pennsylvania woman, 38, tells PEOPLE that she credits Dateability, a dating app focused on the disabled and chronically ill ...

Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is ...

An experimental vaccine showed promise in treating aggressive breast cancer, while a new gene therapy method advances ...

A family's dream became a reality on Friday when Cory Stalling, who lives with muscular dystrophy, received a wheelchair ...

StitchR makes it possible to deliver larger payloads with current vectors, expanding the list of diseases targetable by gene therapies.

StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.

A new technology that delivers two halves of a gene separately could enable gene therapy treatments of muscular dystrophies.

Clinical development and trial testing of vesleteplirsen (SRP-5051) for Duchenne muscular dystrophy (DMD) was stopped, with ...