Harvard Medical School researchers have taken another decisive step in their efforts to develop a gene therapy for people ...
The company, which secured $200 million from investors in a private funding deal last week, learned Tuesday of a serious side ...
Analysts did not seem very concerned by the treatment-related serious adverse event, noting that NGN-401 was well-tolerated ...
The FDA issued its first stamp of approval for a cell or gene therapy back in 2017 to Novartis' Kymriah. | The gene therapy ...
Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is ...
These preclinical findings could lead ... Single-Dose Gene Therapy Is Potentially Life-Changing for Adults With Hemophilia B Sep. 25, 2024 — Adults with hemophilia B saw their number of bleeding ...
StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.
Explore the role and challenges of AAV characterization, the significance of capsid filling, and the best methods to enhance ...
SYNC, its first homegrown CAR-T therapy, one of the first to show promise in treating certain types of brain cancers. This ...