With promise to slow aging and cure some types of cancer, a new gene therapy presents cost and access hurdles for CT patients.

PISCATAWAY, N.J., Nov. 14, 2025 /PRNewswire/ -- On November 20, London will become the global spotlight for cell and gene therapy (CGT) as a Nobel Laureate, scientific leaders, biotech innovators, and ...

As we continue our series exploring genetic medicine, both in this story and in Destiny's Child No Longer: Rewriting Genetic Fate, gene therapy stands at a crossroads. On June 16, Sarepta Therapeutics ...

Genflow Biosciences Ltd (LSE:GENF, OTCQB:GENFF, FRA:WQ5), the European biotechnology company focused on gene therapies for ...

VG801, an investigational gene therapy for ABCA4-associated retinal disease, including Stargardt disease, is being evaluated in an ongoing Phase 1/2 first-in-human clinical trial assessing safety, ...

Early research using CRISPR technology shows dramatic reductions in cholesterol, raising hopes for a future where a single ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain disorders known as SYNGAP1-related disorders, or SRDs. Researchers were able ...

The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...

Collaboration will combine Lexeo expertise in cardiac genetic medicine with Johnson & Johnson’s expertise in cardiovascular therapeutics and circulatory technologies, including Impella™ heart pumps ...

Add Yahoo as a preferred source to see more of our stories on Google. Dr. Derya Unutmaz, a professor of immunology and researcher at the Jackson Laboratory for Genomic Medicine in Farmington, says ...